Funding source: Sanofi Genzyme Austria
Funding source: Takeda (Shire) Austria
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Research funding: Dried blood spot cards were provided by Sanofi and Shire/Takeda.
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Author contributions: All authors have accepted responsibility for the entire content of this manuscript and approved its submission.
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Competing interests: Authors state no conflict of interest.
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Informed consent: Informed consent was obtained from all individuals included in this study.
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Ethical approval: We included patients with GLA variants, who were enrolled in the KarMA study, which is a longitudinal study examining the cardiac changes over time in patients with Fabry disease (unique IRB identifier: 813/2010).
References
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